04/01/2024
A small proof-of-concept trial evaluating motixafortide for stem cell mobilization in sickle cell disease (SCD) has dosed its first patient. https://buff.ly/48JqZ9Z
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A small proof-of-concept trial evaluating motixafortide for stem cell mobilization in sickle cell disease (SCD) has dosed its first patient. https://buff.ly/48JqZ9Z
Columnist Mary Shaniqua was thrilled by the news of the sickle cell "cure," Casgevy, but with time she balanced that emotion with reality. https://buff.ly/3H0LPG4
The holiday season can be rife with triggers for a sickle cell pain crisis. Here's how columnist Oluwatosin Adesoye has learned to manage.
https://buff.ly/3tqp3nL
A scientist behind Casgevy, the gene-editing therapy for sickle cell disease, say its recent approval in the U.S. marks an historic moment.
https://buff.ly/4aoQuPk
After a median of three years of follow-up, 88% of the sickle cell patients evaluated after treatment with Lygenia gene therapy had no VOEs.
https://buff.ly/3tqcMQ6
The holiday season can be rife with triggers for a sickle cell pain crisis. Here's how columnist Oluwatosin Adesoye has learned to manage. https://buff.ly/480q0SG
A European Medicines Agency committee supported Casgevy to treat sickle cell and beta thalassemia; final approval decision due in February. https://buff.ly/3Ny5jW2
As a physician, columnist Sylvia Amuta is a believer in pharmaceutical medicine, but natural remedies have recently caught her attention.
https://buff.ly/486Q3qW
As a physician, columnist Sylvia Amuta is a believer in pharmaceutical medicine, but natural remedies have recently caught her attention. https://buff.ly/41jqMaM
Columnist Oluwatosin Adesoye spent decades denying that her sickle cell disease was a disability. That's common and regrettable, she writes. https://buff.ly/3uZtpmg
After a median of three years of follow-up, 88% of the sickle cell patients evaluated after treatment with Lygenia gene therapy had no VOEs. https://buff.ly/3uTY58v
Here is this week's most-read article featured on our website! Are you caught up?
The CRISPR-based therapy, now called Casgevy, is the first gene-editing therapy for sickle cell disease and a similar blood disorder.
https://buff.ly/4181KeC
The FDA has approved lovotibeglogene autotemcel, a gene therapy from Bluebird Bio known as lovo-cel, for treating SCD patients ages 12 and older who have a history of painful VOCs. Read more: https://bit.ly/48rValZ
Casgevy has become the first cell-based gene therapy employing CRISPR/Cas9, a type of gene-editing technology, to win approval in the U.S. Read more: https://bit.ly/3tbp4M5
Columnist Mary Shaniqua shares the techniques that offer her relief from sickle cell pain, which is especially important as winter nears. https://buff.ly/4a8ZrMG
In red blood cell exchange transfusions, sickled cells are removed from a patient’s blood, then replaced with healthy ones from donors. https://buff.ly/3NcfC20
Advancements in treatment for sickle cell disease are exciting, but not if patients can't access them, writes columnist Oluwatosin Adesoye.
https://buff.ly/3TbR0de
Here is this week's most-read article featured on our website! Are you caught up?
A first person with severe sickle cell is to be treated soon with BEAM-101, a gene editing cell therapy, in an enrolling Phase 1/2 trial.
https://buff.ly/3t87Cbc
As a physician, columnist Sylvia Amuta is a believer in pharmaceutical medicine, but natural remedies have recently caught her attention. https://buff.ly/3R0OofL
Having a child with sickle cell disease can prompt many emotions, including parental guilt, says columnist Oluwatosin Adesoye.
https://buff.ly/3N9hQ1Q
Skin grafts can ease pain associated with leg ulcers, improve wound healing, and reduce the need for pain meds in sickle cell patients, a study finds. https://buff.ly/3uIfT6s
Advancements in treatment for sickle cell disease are exciting, but not if patients can't access them, writes columnist Oluwatosin Adesoye. https://buff.ly/47CYrii
A project designed to test AB Science’s masitinib as a sickle cell treatment has been awarded €9.2 million in public funding in France. https://buff.ly/3sXYbLx
Columnist Dunstan Nicol-Wilson offers some observations as a mentor to children with sickle cell disease, after speaking with their parents. https://buff.ly/49RW4cR
Here is this week's most-read article featured on our website! Are you caught up?
An FDA advisory committee met to discuss the gene editing therapy exa-cel ahead of an expected agency decision in December on its approval.
https://buff.ly/3MYydhE
Columnist Dunstan Nicol-Wilson is driven toward personal growth and better quality of life, but sometimes he needs to push himself to do it.
https://buff.ly/3SRJSTe
The CRISPR-based therapy, now called Casgevy, is the first gene-editing therapy for sickle cell disease and a similar blood disorder. https://buff.ly/3um82el
A first person with severe sickle cell is to be treated soon with BEAM-101,
a gene editing cell therapy, in an enrolling Phase 1/2 trial. https://buff.ly/49GS276
Here is this week's most-read article featured on our website! Are you caught up?
Bluebird announced that it has entered into an advanced agreement to sell the priority review voucher if the FDA does approve lovo-cel.
https://buff.ly/40zZgWh
Young people with kidney failure due to sickle cell disease wait longer for a kidney transplant and have higher mortality, a study found. https://buff.ly/3MQgwkn
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The FDA has approved lovotibeglogene autotemcel, a gene therapy from Bluebird Bio known as lovo-cel, for treating SCD patients ages 12 and older who have a history of painful VOCs. Read more: https://bit.ly/48rValZ #sicklecell #sicklecelldisease #sicklecellanemia #FDAApproval
Casgevy has become the first cell-based gene therapy employing CRISPR/Cas9, a type of gene-editing technology, to win approval in the U.S. Read more: https://bit.ly/3tbp4M5 #sicklecell #sicklecelldisease #sicklecellanemia #FDAApproval
Patient advocate Liza Bernstein explains how #AWindowIntoRare will highlight what we can learn from each other as members of the #raredisease community. Join #BioNews in an online panel discussion + Q&A on #RareDiseaseDay at 3 p.m. EST Feb 28. Register: https://bit.ly/Bionews_RegisterNow
Patient advocate Liza Bernstein gives some insight into what will be discussed during "A Window Into Rare," our #RareDiseaseDay online panel discussion on Feb. 28. Register for this live event here: https://bit.ly/Bionews_RegisterNow #AWindowIntoRare #BioNews
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